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Intravenous administration of brain-targeted stable nucleic acid lipid particles alleviates Machado-Joseph disease neurological phenotype
Conceição M., Mendonça L., Nóbrega C., Gomes C., Costa P., Hirai H., Moreira JN., Lima MC., Manjunath N., Pereira de Almeida L.
DOI
10.1016/j.biomaterials.2015.12.021
Type
Journal article
Journal
Biomaterials
Publisher
Elsevier BV
Publication Date
03/2016
Volume
82
Pages
124 - 137