Intravenous administration of brain-targeted stable nucleic acid lipid particles alleviates Machado-Joseph disease neurological phenotype

Conceição M., Mendonça L., Nóbrega C., Gomes C., Costa P., Hirai H., Moreira JN., Lima MC., Manjunath N., Pereira de Almeida L.

DOI

10.1016/j.biomaterials.2015.12.021

Type

Journal article

Journal

Biomaterials

Publisher

Elsevier BV

Publication Date

03/2016

Volume

82

Pages

124 - 137

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