Identification of potent, muscle-targeting investigational stereo-pure oligonucleotides for exon 53 DMD therapy

Durbin A., Shivalila C., Kothari N., Rinaldi C., McClorey G., Antonijevic I., Byrne M., II DJ., Guo L., Iwamoto N., Liu F., Longo K., Lu G., Nadella P., Purcell-Estabrook E., Standley S., Zhong Z., Zhang J., Wood M., Vargeese C.

DOI

10.1016/j.nmd.2018.06.155

Type

Conference paper

Publication Date

10/2018

Volume

28

Pages

S67 - S67

Permalink Original publication