Search results (85)
« Back to PublicationsMouse survival motor neuron alleles that mimic SMN2 splicing and are inducible rescue embryonic lethality early in development but not late.
Hammond SM. et al, (2010), PLoS One, 5
In vivo biodistribution and efficacy of peptide mediated delivery.
Järver P. et al, (2010), Trends Pharmacol Sci, 31, 528 - 535
Antisense oligonucleotide correction of splice error in cultured ISCU myopathy muscle cells
Sanaker PS. et al, (2010), NEUROMUSCULAR DISORDERS, 20, 676 - 676
Functional rescue of dystrophin-deficient mdx mice by a chimeric peptide-PMO.
Yin H. et al, (2010), Mol Ther, 18, 1822 - 1829
Identification of a novel muscle targeting peptide in mdx mice.
Seow Y. et al, (2010), Peptides, 31, 1873 - 1877
Cellular internalization kinetics of (luciferin-)cell-penetrating peptide conjugates.
Eiríksdóttir E. et al, (2010), Bioconjug Chem, 21, 1662 - 1672
Commercially available outbred mice for genome-wide association studies.
Yalcin B. et al, (2010), PLoS Genet, 6
A method for measuring allele-specific RNAi knock down in SCA7 patient lymphoblasts
Berkowitz D. et al, (2010), JOURNAL OF MEDICAL GENETICS, 47, S83 - S83
PRO-051, an antisense oligonucleotide for the potential treatment of Duchenne muscular dystrophy.
Hammond SM. and Wood MJ., (2010), Curr Opin Mol Ther, 12, 478 - 486
Benign hereditary chorea: clinical and neuroimaging features in an Italian family.
Salvatore E. et al, (2010), Mov Disord, 25, 1491 - 1496
Characterization of bioactive cell penetrating peptides from human cytochrome c: protein mimicry and the development of a novel apoptogenic agent.
Jones S. et al, (2010), Chem Biol, 17, 735 - 744
D-Serine metabolism in C6 glioma cells: Involvement of alanine-serine-cysteine transporter (ASCT2) and serine racemase (SRR) but not D-amino acid oxidase (DAO).
Sikka P. et al, (2010), J Neurosci Res, 88, 1829 - 1840
Erratum: Progress and prospects: Immunobiology of gene therapy for neurodegenerative disease: Prospects and risks (Gene Therapy (2010) 17 (592-605) DOI: 10.1038/gt.2010.2)
McMenamin MM. and Wood MJA., (2010), Gene Therapy, 17
Atorvastatin combined to interferon to verify the efficacy (ACTIVE) in relapsing-remitting active multiple sclerosis patients: a longitudinal controlled trial of combination therapy.
Lanzillo R. et al, (2010), Mult Scler, 16, 450 - 454
In vitro evaluation of novel antisense oligonucleotides is predictive of in vivo exon skipping activity for Duchenne muscular dystrophy.
Wang Q. et al, (2010), J Gene Med, 12, 354 - 364
Optimization of peptide nucleic acid antisense oligonucleotides for local and systemic dystrophin splice correction in the mdx mouse.
Yin H. et al, (2010), Mol Ther, 18, 819 - 827
Progress and prospects: Immunobiology of gene therapy for neurodegenerative disease: prospects and risks.
McMenamin MM. and Wood MJA., (2010), Gene Ther, 17, 448 - 458
RNA-targeted splice-correction therapy for neuromuscular disease.
Wood MJA. et al, (2010), Brain, 133, 957 - 972
Toward an oligonucleotide therapy for Duchenne muscular dystrophy: a complex development challenge.
Wood MJA., (2010), Sci Transl Med, 2