Search results (82)
« Back to PublicationsMouse survival motor neuron alleles that mimic SMN2 splicing and are inducible rescue embryonic lethality early in development but not late.
Journal article
Hammond SM. et al, (2010), PLoS One, 5
In vivo biodistribution and efficacy of peptide mediated delivery.
Journal article
Järver P. et al, (2010), Trends Pharmacol Sci, 31, 528 - 535
Antisense oligonucleotide correction of splice error in cultured ISCU myopathy muscle cells
Conference paper
Sanaker PS. et al, (2010), NEUROMUSCULAR DISORDERS, 20, 676 - 676
Functional rescue of dystrophin-deficient mdx mice by a chimeric peptide-PMO.
Journal article
Yin H. et al, (2010), Mol Ther, 18, 1822 - 1829
Identification of a novel muscle targeting peptide in mdx mice.
Journal article
Seow Y. et al, (2010), Peptides, 31, 1873 - 1877
Elusive copy number variation in the mouse genome.
Journal article
Agam A. et al, (2010), PLoS One, 5
Cellular internalization kinetics of (luciferin-)cell-penetrating peptide conjugates.
Journal article
Eiríksdóttir E. et al, (2010), Bioconjug Chem, 21, 1662 - 1672
Commercially available outbred mice for genome-wide association studies.
Journal article
Yalcin B. et al, (2010), PLoS Genet, 6
A method for measuring allele-specific RNAi knock down in SCA7 patient lymphoblasts
Conference paper
Berkowitz D. et al, (2010), JOURNAL OF MEDICAL GENETICS, 47, S83 - S83
PRO-051, an antisense oligonucleotide for the potential treatment of Duchenne muscular dystrophy.
Journal article
Hammond SM. and Wood MJ., (2010), Curr Opin Mol Ther, 12, 478 - 486
Benign hereditary chorea: clinical and neuroimaging features in an Italian family.
Journal article
Salvatore E. et al, (2010), Mov Disord, 25, 1491 - 1496
Characterization of bioactive cell penetrating peptides from human cytochrome c: protein mimicry and the development of a novel apoptogenic agent.
Journal article
Jones S. et al, (2010), Chem Biol, 17, 735 - 744
D-Serine metabolism in C6 glioma cells: Involvement of alanine-serine-cysteine transporter (ASCT2) and serine racemase (SRR) but not D-amino acid oxidase (DAO).
Journal article
Sikka P. et al, (2010), J Neurosci Res, 88, 1829 - 1840
Erratum: Progress and prospects: Immunobiology of gene therapy for neurodegenerative disease: Prospects and risks (Gene Therapy (2010) 17 (592-605) DOI: 10.1038/gt.2010.2)
Journal article
McMenamin MM. and Wood MJA., (2010), Gene Therapy, 17
Atorvastatin combined to interferon to verify the efficacy (ACTIVE) in relapsing-remitting active multiple sclerosis patients: a longitudinal controlled trial of combination therapy.
Journal article
Lanzillo R. et al, (2010), Mult Scler, 16, 450 - 454
In vitro evaluation of novel antisense oligonucleotides is predictive of in vivo exon skipping activity for Duchenne muscular dystrophy.
Journal article
Wang Q. et al, (2010), J Gene Med, 12, 354 - 364
Optimization of peptide nucleic acid antisense oligonucleotides for local and systemic dystrophin splice correction in the mdx mouse.
Journal article
Yin H. et al, (2010), Mol Ther, 18, 819 - 827
Progress and prospects: Immunobiology of gene therapy for neurodegenerative disease: prospects and risks.
Journal article
McMenamin MM. and Wood MJA., (2010), Gene Ther, 17, 448 - 458
RNA-targeted splice-correction therapy for neuromuscular disease.
Journal article
Wood MJA. et al, (2010), Brain, 133, 957 - 972
Toward an oligonucleotide therapy for Duchenne muscular dystrophy: a complex development challenge.
Journal article
Wood MJA., (2010), Sci Transl Med, 2