Search results (128)
« Back to PublicationsMesyl phosphoramidate backbone modified antisense oligonucleotides targeting miR-21 with enhanced in vivo therapeutic potency.
Patutina OA. et al, (2020), Proc Natl Acad Sci U S A, 117, 32370 - 32379
Evidence that corticofugal propagation of ALS pathology is not mediated by prion-like mechanism.
Scekic-Zahirovic J. et al, (2020), Prog Neurobiol
Cooperation and Interplay between EGFR Signalling and Extracellular Vesicle Biogenesis in Cancer.
Zanetti-Domingues LC. et al, (2020), Cells, 9
Erratum: Context Dependent Effects of Chimeric Peptide Morpholino Conjugates Contribute to Dystrophin Exon-skipping Efficiency (Context Dependent Effects of Chimeric Peptide Morpholino Conjugates Contribute to Dystrophin Exon-skipping Efficiency (2013) 2 (1–10), (S2162253116301834), (10.1038/mtna.2013.51))
Yin HF. et al, (2020), Molecular Therapy - Nucleic Acids, 22
Application of CRISPR-Cas9-Mediated Genome Editing for the Treatment of Myotonic Dystrophy Type 1.
Marsh S. et al, (2020), Mol Ther, 28, 2527 - 2539
Mutation-independent Proteomic Signatures of Pathological Progression in Murine Models of Duchenne Muscular Dystrophy.
van Westering TLE. et al, (2020), Mol Cell Proteomics, 19, 2047 - 2068
Mechanisms of Action of EGFR Tyrosine Kinase Receptor Incorporated in Extracellular Vesicles.
Zanetti-Domingues LC. et al, (2020), Cells, 9
A Single Amino Acid Residue Regulates PTEN-Binding and Stability of the Spinal Muscular Atrophy Protein SMN.
Rademacher S. et al, (2020), Cells, 9
Human muscle signaling responses to 3-day head-out dry immersion
Vilchinskaya NA. et al, (2020), The Journal of Musculoskeletal and Neuronal Interactions, 15
Advances in oligonucleotide drug delivery.
Roberts TC. et al, (2020), Nat Rev Drug Discov, 19, 673 - 694
An ALS-linked mutation in TDP-43 disrupts normal protein interactions in the motor neuron response to oxidative stress.
Feneberg E. et al, (2020), Neurobiol Dis, 144
Relative contribution of ancient woodland indicator and non-indicator species to herb layer distinctiveness in ancient semi-natural, ancient replanted, and recent woodland
Swallow KA. et al, (2020), Applied Vegetation Science, 23, 471 - 481
Mutation-independent proteomic signatures of pathological progression in murine models of Duchenne muscular dystrophy.
van Westering TLE. et al, (2020), Mol Cell Proteomics
Efficient Doxorubicin Loading to Isolated Dexosomes of Immature JAWSII Cells: Formulated and Characterized as the Bionanomaterial.
Mutlu EC. et al, (2020), Materials (Basel), 13
Absence of subcerebral projection neurons is beneficial in a mouse model of ALS.
Burg T. et al, (2020), Ann Neurol
Combined Treatment with Peptide-Conjugated Phosphorodiamidate Morpholino Oligomer-PPMO and AAV-U7 Rescues the Severe DMD Phenotype in Mice
Forand A. et al, (2020), Molecular Therapy - Methods and Clinical Development, 17, 695 - 708
Novel EGFP reporter cell and mouse models for sensitive imaging and quantification of exon skipping
Hara Y. et al, (2020), Scientific Reports