Search results (124)
« Back to PublicationsMesyl phosphoramidate backbone modified antisense oligonucleotides targeting miR-21 with enhanced in vivo therapeutic potency.
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Patutina OA. et al, (2020), Proc Natl Acad Sci U S A, 117, 32370 - 32379
Evidence that corticofugal propagation of ALS pathology is not mediated by prion-like mechanism.
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Scekic-Zahirovic J. et al, (2020), Prog Neurobiol
Cooperation and Interplay between EGFR Signalling and Extracellular Vesicle Biogenesis in Cancer.
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Zanetti-Domingues LC. et al, (2020), Cells, 9
Erratum: Context Dependent Effects of Chimeric Peptide Morpholino Conjugates Contribute to Dystrophin Exon-skipping Efficiency (Context Dependent Effects of Chimeric Peptide Morpholino Conjugates Contribute to Dystrophin Exon-skipping Efficiency (2013) 2 (1–10), (S2162253116301834), (10.1038/mtna.2013.51))
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Yin HF. et al, (2020), Molecular Therapy - Nucleic Acids, 22
Application of CRISPR-Cas9-Mediated Genome Editing for the Treatment of Myotonic Dystrophy Type 1.
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Marsh S. et al, (2020), Mol Ther, 28, 2527 - 2539
Mutation-independent Proteomic Signatures of Pathological Progression in Murine Models of Duchenne Muscular Dystrophy.
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van Westering TLE. et al, (2020), Mol Cell Proteomics, 19, 2047 - 2068
Mechanisms of Action of EGFR Tyrosine Kinase Receptor Incorporated in Extracellular Vesicles.
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Zanetti-Domingues LC. et al, (2020), Cells, 9
A Single Amino Acid Residue Regulates PTEN-Binding and Stability of the Spinal Muscular Atrophy Protein SMN.
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Rademacher S. et al, (2020), Cells, 9
Human muscle signaling responses to 3-day head-out dry immersion
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Vilchinskaya NA. et al, (2020), The Journal of Musculoskeletal and Neuronal Interactions, 15
Advances in oligonucleotide drug delivery.
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Roberts TC. et al, (2020), Nat Rev Drug Discov, 19, 673 - 694
An ALS-linked mutation in TDP-43 disrupts normal protein interactions in the motor neuron response to oxidative stress.
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Feneberg E. et al, (2020), Neurobiol Dis, 144
Relative contribution of ancient woodland indicator and non-indicator species to herb layer distinctiveness in ancient semi-natural, ancient replanted, and recent woodland
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Swallow KA. et al, (2020), Applied Vegetation Science, 23, 471 - 481
Mutation-independent proteomic signatures of pathological progression in murine models of Duchenne muscular dystrophy.
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van Westering TLE. et al, (2020), Mol Cell Proteomics
Efficient Doxorubicin Loading to Isolated Dexosomes of Immature JAWSII Cells: Formulated and Characterized as the Bionanomaterial.
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Mutlu EC. et al, (2020), Materials (Basel), 13
Absence of subcerebral projection neurons is beneficial in a mouse model of ALS.
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Burg T. et al, (2020), Ann Neurol
Combined Treatment with Peptide-Conjugated Phosphorodiamidate Morpholino Oligomer-PPMO and AAV-U7 Rescues the Severe DMD Phenotype in Mice
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Forand A. et al, (2020), Molecular Therapy - Methods and Clinical Development, 17, 695 - 708
Novel EGFP reporter cell and mouse models for sensitive imaging and quantification of exon skipping
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Hara Y. et al, (2020), Scientific Reports