Timing matters: exon skipping therapy is most effective when initiated early in a mouse model of Duchenne muscular dystrophy

Stenler S., Huang J., van Westering TLE., Coenen-Stass AML., Krjutškov K., Andaloussi SEL., Wood MJA., Roberts TC.

DOI

10.64898/2025.12.23.696144

Type

Preprint

Publication Date

2025-12-25T00:00:00+00:00

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