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Timing matters: exon skipping therapy is most effective when initiated early in a mouse model of Duchenne muscular dystrophy
Stenler S., Huang J., van Westering TLE., Coenen-Stass AML., Jad Y., Krjutškov K., Andaloussi SEL., Wood MJA., Roberts TC.
DOI
10.1016/j.omtn.2026.103017
Type
Journal article
Publisher
Elsevier BV
Publication Date
2026-07-01T00:00:00+00:00
Pages
103017 - 103017
Total pages
0